Description

Families of Spinal Muscular Atrophy funds anddirects the leading SMA research programs to develop a treatmentand cure for the disease. The successful results and progress thatthe organization has delivered, from basic research to drugdiscovery to clinical trials, provide real hope for families andpatients impacted by the disease. The charity has invested over $50million in research and has been involved in funding half of allthe ongoing novel drug programs for SMA.

Families of Spinal Muscular Atrophy is dedicated to creating atreatment and cure by:
- Funding and advancing a comprehensive research program;
- Supporting SMA families through networking, information andservices;
- Improving care for all SMA patients;
- Educating health professionals and the public about SMA;
- Enlisting government support for SMA;
- Embracing all touched by SMA in a caring community.
Our vision is a world where Spinal Muscular Atrophy is treatableand curable.